$QURE (uniQure N.V.) — investor discussion on X

I spoke with Lauren Holder, a Huntington's patient and advocate, about this week's $QURE AMT-130 gene therapy clinical update. “I’m not surprised by the four-year results because this isn’t a cure,” Holder told me. “This is a slowing-of-disease-progression treatment, and so I wou

Likely scenario: $QURE AdCom will result in AA recommendation Eventually could get traditional full approval given stat sig on TFC primary endpoint for confirmatory trial Would be insane if they just got full approval off the bat given TFC stat sig at 4Y